CRISPR; genetic engineering; DNA; double-strand breaks; Parkinson's disease; Huntington's disease; Rett syndrome; muscular dystrophy
Genome Editing in Neurosciences
Genome Editing The Next Step in Gene Therapy
Gene Delivery and Therapy for Neurological Disorders
Inherited Neuromuscular Diseases Translation from Pathomechanisms to Therapies
Gene Transfer and Therapy in the Nervous System
Neurodegenerative Diseases
Targeted Genome Editing Using Site-Specific Nucleases ZFNs, TALENs, and the CRISPR/Cas9 System
Gene Therapy for Neurological Disorders Methods and Protocols
Stem Cells in Neuroendocrinology
Gene Therapy for Neurological Disorders and Brain Tumors (Contemporary Neuroscience)